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Collecting clinical data in primary ciliary dyskinesia- challenges and opportunities [version 1; referees: 2 approved]
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Roth, Yehudah, Mussaffi, Huda, Lavie, Moran, Omran, Heymut, Rivlin, Joseph, Cohen-Cymberknoh, Malena, Alias, Nael, Soferman, Ruth, Goldberg, Shmuel, Luder, Anthony, Picard, Elie, Elizur, Arnon, Blau, Hannah, Livnat, Galit, Werner, Claudius, Olbrich, Heike, Roduta Roberts, Mary, Shoseyov, David, Kerem, Eitan, Loges, Niki T., Alkrinawi, Soliman, Ben-Ami, Marta, Aviram, Micha, Avital, Avraham, Hevroni, Avigdor, Amirav, Israel, Wallmeier, Julia, Springer, Chaim, Bentur, Lea, Dabbah, Husein, Mandelberg, Avigdor, Raidt, Johanna, Rotschild, Moshe, Abitbul, Revital
Rationale: Primary ciliary dyskinesia (PCD) is under diagnosed and underestimated. Most clinical research has used some form of questionnaires to capture data but none has been critically evaluated particularly with respect to its end-user feasibility and utility. Objective: To critically...